The FDA has approved a groundbreaking gene therapy for a rare genetic skin disorder called recessive dystrophic epidermolysis bullosa (RDEB).…
Browsing: GeneTherapy
The FDA has granted approval for a groundbreaking cell-based gene therapy aimed at treating recessive dystrophic epidermolysis bullosa (RDEB), a…
The FDA has approved a groundbreaking gene therapy for macular telangiectasia type 2 (MacTel), a rare eye disease that leads…
Batten disease, a rare and devastating neurodegenerative disorder, affects children and leads to severe physical and mental deterioration. While there…
Funmi Dasaolu, a determined 31-year-old university student from Oxfordshire, is among those who can now look forward to a future…